1 year ago
Gene therapy restored immune system in children with rare disorder
Children born without a working immune system due to a rare genetic disorder called Artemis-deficient severe combined immunodeficiency (Artemis-deficient SCID) may be able to lead normal lives thanks to a new gene-replacement therapy. A trial found that the therapy either partially or fully restored the immune systems of 10 infants with the condition.
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https://www.newscientist.com
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